Listado de ensayos


Dose-escalation Study to Evaluate the Safety and Tolerability of GS030 in Subjects With Retinitis Pigmentosa

Estado: | Categoría: | Resultado:

Patología

Non-syndromic RETINOSIS PIGMENTARIA

Tratamiento

Combination Product: Gene therapy: GS030-DP AND Medical device: GS030- MD

Localizaciones

UPMC Eye Center, Pittsburgh, Pennsylvania, United States Centre Hospitalier National d'Ophtalmologie (CHNP) des Quinze-Vingts, Paris, France Moorfields Eye Hospital NHS Foundation Trust, 162 City Road, London, United Kingdom
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Clinical Evaluation of Patients With X-linked RETINOSIS PIGMENTARIA (XLRP)

Estado: | Categoría: | Resultado:

Patología

X-Linked RETINOSIS PIGMENTARIA

Localizaciones

Duke Eye Center, Duke University Medical Center, Durham, North Carolina, United States Casey Eye Institute, Oregon Health and Sciences University, Portland, Oregon, United States Retina Foundation of the Southwest, Dallas, Texas, United States
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Natural History Study of Patients With X-linked Retinal Dystrophy Associated With Mutations in Retinitis Pigmentosa GTPase Regulator (RPGR)

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA

Localizaciones

Shiley Eye Institute - UCSD, La Jolla, California, United States Emory Eye Centre, Atlanta, Georgia, United States Massachusetts Eye and Ear Infirmary, Boston, Massachusetts, United States Kellogg Eye Center, Ann Arbor, Michigan, United States UPMC Eye Centre, Pittsburgh, Pennsylvania, United States The Hospital for Sick Children, Toronto, Canada Moorfields Eye Hospital, London, United Kingdom
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Safety and Efficacy of rAAV2tYF-GRK1-RPGR in Subjects With X-linked Retinitis Pigmentosa Caused by RPGR Mutations

Estado: | Categoría: | Resultado:

Patología

X-Linked RETINOSIS PIGMENTARIA

Tratamiento

Biological: rAAV2tYF-GRK1-RPGR

Localizaciones

University of Florida, Jacksonville, Florida, United States Boston Children's Hospital, Boston, Massachusetts, United States Columbia University, New York, New York, United States Duke Eye Center, Durham, North Carolina, United States Cincinnati Eye Institute, Cincinnati, Ohio, United States Casey Eye Institute, Oregon Health and Science University, Portland, Oregon, United States Retina Foundation of the Southwest, Dallas, Texas, United States
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CNS10-NPC for the Treatment of RP

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA

Tratamiento

Biological: CNS10-NPC implantation

Localizaciones

Retina-Vitreous Associates Medical Group, Beverly Hills, California, United States
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CNGB1 and Allied Disorders

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA Associated With CNGB1 Mutations

Tratamiento

Other: No intervention, this is a natural history progression study

Localizaciones

Dr. Stephen H. Tsang, New York, New York, United States Wills Eye Hospital, Philadelphia, Pennsylvania, United States Institut de la Vision/Centre de maladies rares du Centre Hospitalier National Ophtalmologique des Quinze-Vingts, Paris, France Klinikum der Universit t M nchen University Eye Hospital, Ludwig-Maximilians-University (LMU) Munich, M nchen, Bavaria, Germany Eberhard Karls University Tubingen, Tuebingen, Germany Moorfields Eye Hospital NHS Foundation Trust, London, United Kingdom
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Prospective Natural History Study of Retinitis Pigmentosa

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA

Tratamiento

Other: Ophthalmic examination Other: Mobility Test

Localizaciones

CHNO XV-XX Paris - CIC 1423, Paris, France
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A Natural History Study to Evaluate Functional and Anatomical Progression in Retinitis Pigmentosa

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA

Localizaciones

Wilmer Eye Institute at Johns Hopkins University, Baltimore, Maryland, United States
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Retinitis Pigmentosa Clinical Measures and Repeatability Testing of Potential Outcome Measures

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA

Tratamiento

Device: RetMAP RM electrode Device: RetiMap Multifocal ERG Device: rtx1 Adaptive Optics camera

Localizaciones

National Institutes of Health Clinical Center, Bethesda, Maryland, United States
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