Listado de ensayos


Safety and Efficacy of rAAV2tYF-GRK1-RPGR in Subjects With X-linked Retinitis Pigmentosa Caused by RPGR Mutations

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA LIGADA A X

Tratamiento

Biological: rAAV2tYF-GRK1-RPGR

Localizaciones

University of Florida, Jacksonville, Florida, United States Columbia University, New York, New York, United States Duke Eye Center, Durham, North Carolina, United States Cincinnati Eye Institute, Cincinnati, Ohio, United States Casey Eye Institute, Oregon Health and Science University, Portland, Oregon, United States Retina Foundation of the Southwest, Dallas, Texas, United States
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Long Term Follow-Up Gene Therapy Study for XLRP RPGR

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA LIGADA A X

Tratamiento

Biological: AAV-RPGR

Localizaciones

Moorfields Eye Hospital, London, United Kingdom
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Natural History of the Progression of X-Linked RETINOSIS PIGMENTARIA

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA LIGADA A X

Tratamiento

Other: Other: Assessments

Localizaciones

Research Site, Phoenix, Arizona, United States Research Site, Los Angeles, California, United States Research Site, San Francisco, California, United States Research Site, Miami, Florida, United States Research Site, New York, New York, United States Research Site, Portland, Oregon, United States Research Site, Dallas, Texas, United States Research Site, Houston, Texas, United States Research Site, Salt Lake City, Utah, United States Research Site, Madison, Wisconsin, United States and 12 more
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4D-125 in Patients With X-Linked Retinitis Pigmentosa (XLRP)

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA LIGADA A X

Tratamiento

Biological: 4D-125 IVT Injection Other: Observational

Localizaciones

University of Colorado, Aurora, Colorado, United States University of Michigan Kellogg Eye Center, Ann Arbor, Michigan, United States Duke University Eye Center/Dept. of Ophthalmology, Durham, North Carolina, United States Casey Eye Institute, Oregon Health and Science University, Portland, Oregon, United States Retina Foundation of the Southwest, Dallas, Texas, United States University of Utah John A. Moran Eye Center, Salt Lake City, Utah, United States
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Gene Therapy Trial for the Treatment of X-linked RETINOSIS PIGMENTARIA Associated With Variants in the RPGR Gene

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA LIGADA A X

Tratamiento

Biological: Genetic: AAV5-RPGR

Localizaciones

Vitreol Retinal Associates, Gainesville, Florida, United States The Emory Eye Centre, Atlanta, Georgia, United States Boston Eye and Ear, Boston, Massachusetts, United States University of Michigan, Ann Arbor, Michigan, United States Retinal Consultants of Houston, Bellaire, Texas, United States
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Oral Metformin for Treatment of ABCA4 Retinopathy

Estado: | Categoría: | Resultado:

Patología

ABCA4 Retinopathy ENFERMEDAD DE STARGARDT Retinal Dystrophy Retinal Degeneration

Tratamiento

MEDICAMENTO: Metformin hydrochloride

Localizaciones

National Institutes of Health Clinical Center, Bethesda, Maryland, United States
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Visual Performance Measures in a Virtual Reality Environment for Assessing Clinical Trial Outcomes in Those With Severely Reduced Vision

Estado: | Categoría: | Resultado:

Patología

Low Vision Retinitis Pigmentosa ENFERMEDAD DE STARGARDT 1 ENFERMEDAD DE STARGARDT 3 ENFERMEDAD DE STARGARDT 4 Albinism

Tratamiento

Device: Virtual Reality Headset based tests

Localizaciones

NI Clinical Research Facility, Belfast, Northern Ireland, United Kingdom
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Stem Cell Ophthalmology Treatment Study II

Estado: | Categoría: | Resultado:

Patología

Retinal Disease Age-Related Macular Degeneration Retinitis Pigmentosa ENFERMEDAD DE STARGARDT Optic Neuropathy Nonarteritic Ischemic Optic Neuropathy Optic Atrophy Optic Nerve Disease Glaucoma Leber Hereditary Optic Neuropathy and 8 more

Tratamiento

Procedure: Arm 1 Procedure: Arm 2 Procedure: Arm 3

Localizaciones

MD Stem Cells, Westport, Connecticut, United States MD Stem Cells, Coral Springs, Florida, United States Fakeeh University Hospital, Dubai, United Arab Emirates
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Inherited Retinal Degenerative Disease Registry

Estado: | Categoría: | Resultado:

Patología

Eye Diseases Hereditary Retinal Disease Achromatopsia Bardet-Biedl Syndrome Bassen-Kornzweig Syndrome Batten Disease Best Disease Choroidal Dystrophy Choroideremia Cone Dystrophy and 18 more

Localizaciones

Foundation Fighting Blindness, Columbia, Maryland, United States
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Rod and Cone Mediated Function in Retinal Disease

Estado: | Categoría: | Resultado:

Patología

Retinal Degeneration Retinitis Pigmentosa ENFERMEDAD DE STARGARDT

Tratamiento

Device: Medmont Darl Adapted Chromatic (DAC) Device: RetMap, RM Electrode Device: MonCvONE electrophysiology

Localizaciones

National Institutes of Health Clinical Center, 9000 Rockville Pike, Bethesda, Maryland, United States
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