Listado de ensayos


Natural History Study of Patients With X-linked Retinal Dystrophy Associated With Mutations in Retinitis Pigmentosa GTPase Regulator (RPGR)

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA

Localizaciones

Shiley Eye Institute - UCSD, La Jolla, California, United States Emory Eye Centre, Atlanta, Georgia, United States Massachusetts Eye and Ear Infirmary, Boston, Massachusetts, United States Kellogg Eye Center, Ann Arbor, Michigan, United States UPMC Eye Centre, Pittsburgh, Pennsylvania, United States The Hospital for Sick Children, Toronto, Canada Moorfields Eye Hospital, London, United Kingdom
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Safety and Efficacy of rAAV2tYF-GRK1-RPGR in Subjects With X-linked Retinitis Pigmentosa Caused by RPGR Mutations

Estado: | Categoría: | Resultado:

Patología

X-Linked RETINOSIS PIGMENTARIA

Tratamiento

Biological: rAAV2tYF-GRK1-RPGR

Localizaciones

University of Florida, Jacksonville, Florida, United States Boston Children's Hospital, Boston, Massachusetts, United States Columbia University, New York, New York, United States Duke Eye Center, Durham, North Carolina, United States Cincinnati Eye Institute, Cincinnati, Ohio, United States Casey Eye Institute, Oregon Health and Science University, Portland, Oregon, United States Retina Foundation of the Southwest, Dallas, Texas, United States
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CNS10-NPC for the Treatment of RP

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA

Tratamiento

Biological: CNS10-NPC implantation

Localizaciones

Retina-Vitreous Associates Medical Group, Beverly Hills, California, United States
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CNGB1 and Allied Disorders

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA Associated With CNGB1 Mutations

Tratamiento

Other: No intervention, this is a natural history progression study

Localizaciones

Dr. Stephen H. Tsang, New York, New York, United States Wills Eye Hospital, Philadelphia, Pennsylvania, United States Institut de la Vision/Centre de maladies rares du Centre Hospitalier National Ophtalmologique des Quinze-Vingts, Paris, France Klinikum der Universit t M nchen University Eye Hospital, Ludwig-Maximilians-University (LMU) Munich, M nchen, Bavaria, Germany Eberhard Karls University Tubingen, Tuebingen, Germany Moorfields Eye Hospital NHS Foundation Trust, London, United Kingdom
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Safety and Efficacy Study in Patients With RETINOSIS PIGMENTARIA Due to Mutations in PDE6B Gene

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA

Tratamiento

Biological: AAV2/5-hPDE6B

Localizaciones

Clinique Ophtalmologique, CHU de Nantes, Nantes, France
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Oral Hydroxychloroquine (HCQ) for Retinitis Pigmentosa Caused by P23H- Rhodopsin (RHO)

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA

Tratamiento

Drug: Hydroxychloroquine lower dose Drug: Hydroxychloroquine higher dose

Localizaciones

University of Michigan, Ann Arbor, Michigan, United States
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Natural History Study of Retinitis Pigmentosa Type 11

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA 11 RETINOSIS PIGMENTARIA

Tratamiento

Diagnostic Test: Clinical examinations

Localizaciones

Department of Ophthalmology, Oslo University Hospital, Oslo, Norway
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Safety and Efficacy of Subretinal Transplantation of Clinical Human Embryonic Stem Cell Derived Retinal Pigment Epitheliums in Treatment of Retinitis Pigmentosa

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA

Tratamiento

Biological: Retinal pigment epitheliums transplantation

Localizaciones

Beijing Tongren Hospitol,Capital Medical University, Beijing, Beijing, China
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Safety and Tolerability of hRPC in Retinitis Pigmentosa

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA

Tratamiento

Drug: hRPC

Localizaciones

Retinal Research Institute, Phoenix, Arizona, United States Massachusetts Eye and Ear Infirmary, Boston, Massachusetts, United States Oregon Health and Science University, Portland, Oregon, United States Institut de la M cula, Barcelona, Spain Oxford Eye Hospital, Oxford, United Kingdom
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Natural History of the Progression of X-Linked RETINOSIS PIGMENTARIA

Estado: | Categoría: | Resultado:

Patología

X-Linked RETINOSIS PIGMENTARIA

Tratamiento

Other: Other: Assessments

Localizaciones

Research Site, Phoenix, Arizona, United States Research Site, Los Angeles, California, United States Research Site, San Francisco, California, United States Research Site, Miami, Florida, United States Research Site, New York, New York, United States Research Site, Portland, Oregon, United States Research Site, Dallas, Texas, United States Research Site, Houston, Texas, United States Research Site, Salt Lake City, Utah, United States Research Site, Madison, Wisconsin, United States and 12 more
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