A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US
Estado: Activo no reclutando |
Categoría: Retinosis pigmentaria |
Resultado: No tiene resultados Confirmed Biallelic RPE65 Mutation- associated Retinal Dystrophy
Biological: AAV2-hRPE65v2,voretigene neparvovec-rzyl
Children's Hospital of Los Angeles, Los Angeles, California, United States
Bascom Palmer Eye Institute, Miami, Florida, United States
University of Iowa Hospitals & Clinics, Iowa City, Iowa, United States
Massachusetts Eye and Ear Institute, Boston, Massachusetts, United States
Kellogg Eye Center, Ann Arbor, Michigan, United States
Cincinnati Eye Institute, Cincinnati, Ohio, United States
Casey Eye Institute, Portland, Oregon, United States
Children's Hospital of Philadelphia (CHOP), Philadelphia, Pennsylvania, United States
Scheie Eye Institute, Philadelphia, Pennsylvania, United States
Cullen Eye Institute, Houston, Texas, United States
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