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A Study to Determine the Long-Term Safety, Tolerability and Biological Activity of SAR421869 in Patients With Usher Syndrome Type 1B

Estado: | Categoría: | Resultado:

Patología

Usher's Syndrome

Tratamiento

Drug: Blood draw for the laboratory assessment

Localizaciones

Investigational Site Number 840001, Portland, Oregon, United States Investigational Site Number 250001, Paris, France
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Safety and Efficacy Study in Subjects With Leber Congenital Amaurosis

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Patología

Inherited Retinal Dystrophy Due to RPE65 Mutations Leber Congenital Amaurosis

Tratamiento

Biological: AAV2-hRPE65v2,voretigene neparvovec-rzyl

Localizaciones

University of Iowa, Iowa City, Iowa, United States Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
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Rate of Progression in USH2A-related Retinal Degeneration

Estado: | Categoría: | Resultado:

Patología

Usher Syndrome, Type 2A RETINOSIS PIGMENTARIA 39

Localizaciones

University of California, San Francisco, San Francisco, California, United States Vitreo-Retinal Associates, Gainesville, Florida, United States Wilmer Eye Institute at Johns Hopkins, Baltimore, Maryland, United States Massachusetts Eye and Ear, Boston, Massachusetts, United States Kellogg Eye Center, University of Michigan, Ann Arbor, Michigan, United States Duke University Eye Center, Durham, North Carolina, United States OHSU Casey Eye Institute, Portland, Oregon, United States Retina Foundation of the Southwest, Dallas, Texas, United States Baylor Eye Physicians and Surgeons, Houston, Texas, United States Moran Eye Center, University of Utah, Salt Lake City, Utah, United States and 6 more
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Advancing Understanding of Transportation Options

Estado: | Categoría: | Resultado:

Patología

Diabetic Retinopathy Macular Degeneration Glaucoma RETINOSIS PIGMENTARIA Vision Disorders Acute Coronary Syndrome Implantable Defibrillator User Congestive Heart Failure Hypertrophic Obstructive Cardiomyopathy Orthostatic Hypotension and 22 more

Tratamiento

Behavioral: Driving Decision Aid Behavioral: Older Drivers Website

Localizaciones

University of California, San Diego, La Jolla, California, United States CU Anschutz Medical Center, Aurora, Colorado, United States Indiana University, Indianapolis, Indiana, United States
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A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US

Estado: | Categoría: | Resultado:

Patología

Confirmed Biallelic RPE65 Mutation- associated Retinal Dystrophy

Tratamiento

Biological: AAV2-hRPE65v2,voretigene neparvovec-rzyl

Localizaciones

Children's Hospital of Los Angeles, Los Angeles, California, United States Bascom Palmer Eye Institute, Miami, Florida, United States University of Iowa Hospitals & Clinics, Iowa City, Iowa, United States Massachusetts Eye and Ear Institute, Boston, Massachusetts, United States Kellogg Eye Center, Ann Arbor, Michigan, United States Cincinnati Eye Institute, Cincinnati, Ohio, United States Casey Eye Institute, Portland, Oregon, United States Children's Hospital of Philadelphia (CHOP), Philadelphia, Pennsylvania, United States Scheie Eye Institute, Philadelphia, Pennsylvania, United States Cullen Eye Institute, Houston, Texas, United States
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New Enrollment Post-Approval Study of the Argus II Retinal Prosthesis System

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA

Localizaciones

University of Southern California, Los Angeles, California, United States University of Colorado, Denver, Denver, Colorado, United States U. of Miami, Bascom Palmer Eye Institute, Miami, Florida, United States University of Miami Bascom Palmer Eye Institute, Miami, Florida, United States Emory University, Atlanta, Georgia, United States Retina Consultants of Hawaii, 'Aiea, Hawaii, United States University of Illinois at Chicago, Chicago, Illinois, United States Johns Hopkins, Lions Vision Center, Baltimore, Maryland, United States Tufts Medical Center, Boston, Massachusetts, United States University of Michigan, Kellogg Eye Center, Ann Arbor, Michigan, United States and 7 more
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Repository for Inherited Eye Diseases

Estado: | Categoría: | Resultado:

Patología

RETINOSIS PIGMENTARIA Inherited Ophthalmic Diseases

Localizaciones

University of California, San Francisco, San Francisco, California, United States National Institutes of Health Clinical Center, 9000 Rockville Pike, Bethesda, Maryland, United States
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